Pioneers in Rare
Disease Medicine
Through research and development, Alexion leads in the delivery of transformative medicines for rare diseases because rare does not mean forgotten.

Building a better tomorrow for our patients, every day.
Healthcare Professional Log In Patient Support Programs
Learn more about Alexion’s portfolio of rare disease medicines and the conditions they treat
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CLINICAL CHARACTERISTICS

Learn more about the rare diseases we treat and how to recognize and best care for patients in your clinical practice

PRODUCTS

Explore the details about Alexion products available to treat rare diseases in Canada

PATIENT SUPPORT PROGRAMS

See how our programs support you and your patients throughout the treatment journey

RESOURCES

Find a library of resources available to support you and your patients with rare disease

GETTING STARTED

Review recommended steps for getting a patient started with one of our treatments

30+ Years Dedicated to Discovery for Our Patients, and the Work Continues
There are 7000+ known rare diseases in the world
Only 5% have available treatment options
Our Research Pipeline

Bill

Only the second patient at his hospital ever diagnosed with paroxysmal nocturnal hemoglobinuria (PNH), Bill pushed through with frequent blood transfusions and hospitalization, until finding a new treatment that worked.
PNH

Donnan

For 12 years, Donnan experienced unexplained health issues. It took a kidney transplant from his wife before a doctor finally diagnosed atypical hemolytic uremic syndrome (aHUS).
aHUS

I was very blessed to have a doctor who knew what she was looking at… I can chase my kids and play again.

DONNAN

Roberta

Unable even to write or brush her hair, generalized Myasthenia gravis (gMG) forced Roberta to drop out of nursing school. After years of different therapies, she has now finished nursing school and is working full time.
gMG
Let Stories Like These Inspire You Too
Alexion specialists can help make sense of health insurance coverage, answer questions about treatment, and connect patients to community resources.
OneSource™ provides one-on-one support for people living with PNH, aHUS, gMG, and NMOSD
To enroll a patient now:
aHUS PNH gMG NMOSD NF1
The Metabolic Assistance Program (MAP): Helping patients with HPP and LAL-D
To enroll a patient now:
HPP MAP LAL-D MAP

My case manager from OneSource™ was in contact with me weekly. She basically was there for me, just to help me with my questions.

RACHEL, LIVING WITH gMG

No-charge programs that provide education, access assistance, and ongoing treatment support for patients, families, and healthcare providers
Log in to learn more about the benefits of OneSource™
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You can also learn more about our patient support programs by contacting us or calling:
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